• Duchenne Muscular Dystrophy (DMD) - …
  • DMD Fund - Duchenne Muscular Dystrophy Info
  • Duchenne muscular dystrophy « Dilfuza’s Weblog

What is Duchenne muscular dystrophy? Duchenne muscular dystrophy (DMD) is a genetic disorder characterized by progressive muscle degeneration and weakness. It …

A Breakthrough in Duchenne Muscular Dystrophy | …

Duchenne Muscular Dystrophy (DMD) Respiratory Issues

Learn about Duchenne Muscular Dystrophy Research at Nationwide Children's Hospital.
There is no treatment, and no cure for Duchenne Muscular Dystrophy – it is 100% fatal.



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TREAT-NMD is a major initiative in the neuromuscular field that is creating the infrastructure to ensure that the most promising new therapies reach patients as quickly as possible.

Duchenne muscular dystrophy Archives - Muscular Dystrophy …

duchenne muscular dystrophy | Muscular Dystrophy - …
This test is the most reliable way to diagnose Duchenne MD, and distinguish it from the other inflammatory disorders, and from other Muscular Dystrophies.

DNA testing (using blood cells or muscle cells) remains the best way to obtain exact genetic information leading to a conclusive Duchenne MD diagnosis.

 

2006-12-05 · Duchenne Muscular Dystrophy

Duchenne Muscular Dystrophy-Adult - Hopkins Medicine
“My wife Dana and I have a son, James, who is now 19 and suffering from Duchenne Muscular Dystrophy, the world’s number-one lethal childhood genetic disorder. From the age of two and a half when he was diagnosed, James has been treated daily with corticosteroids. On the one hand, it is unquestionable that these steroids have prolonged his muscle function and thus his life. But on the other, James has paid a dear price with the side effects of these steroids, including brittle bones and fractures, and very short stature.


“We are thrilled at the announcement that Vamorolone, a drug that could be a game-changer in the disease world of Duchenne Muscular Dystrophy, will be developed via a major deal with Actelion – a very successful and growing international biopharmaceutical company. The Foundation to Eradicate Duchenne has supported investigation on this drug since its inception via our scientific advisor, Dr. Eric Hoffman and his team of medical researchers at ReveraGen Biopharma. While there are a number of hurdles remaining before Vamorolone becomes an approved drug in the marketplace, the substantial assets that Actelion brings to the table will power the trials and development necessary to prove its efficacy.


Duchenne Muscular Dystrophy | CDISC

Key missions include building and supporting a state of the art multidisciplinary care program for children and adults with muscular dystrophy, building and supporting a clinical trials infrastructure to accelerate clinical investigation into new treatments, and the support of translational biomedical research relevant to muscular dystrophy.


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Duchenne Muscular Dystrophy is a relentless, cruel disease

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The UCLA Duchenne Muscular Dystrophy Center Fund is intended to support Duchenne related muscular dystrophy translational research and clinical care at UCLA.

Duchenne Muscular Dystrophy Charity | Action Medical …

Duchenne Muscular Dystrophy is a relentless, cruel disease. It is the world’s #1 lethal childhood genetic disorder. The Foundation to Eradicate Duchenne (FED) exists to fund scientific research for treatments for today’s generation of boys and young men who suffer from Duchenne.

Duchenne Muscular Dystrophy: Symptoms, Diagnosis, …




DuchenneConnect serves as a central hub linking the resources and needs of the Duchenne/Becker muscular dystrophy community: young men with Duchenne; their families and caregivers; and the provider community: clinical care providers, policymakers, industry professionals and the medical research fields.

Causes/Inheritance Cause of DMD

In the future, as this type of testing becomes more commonplace, it will lead to faster diagnosis of all Muscular Dystrophies.

DNA is supremely important.